Gene therapy in Glycogen Storage Disorders
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Dr Dwight Koeberl joins the podcast to provide some background to gene therapies in Glycogen Storage Disorders, hi-light some ongoing studies and explain why we owe at least some of our knowledge to a menagerie of animal models. Gene therapy for glycogen storage diseases Dwight D. Koeberl, et al https://doi.org/10.1002/jimd.12654
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